GM1 gangliosidosis

GM1 gangliosidosis (sometimes known as Landing disease) is an inherited lysosomal storage disorder that destroys nerve cells in the brain and spinal cord. Researchers have classified the condition into three major types based on the age when symptoms first appear: infantile (type 1), juvenile (type 2) and adult onset or chronic (type 3). Type 1 appears around the age of six months and is the most severe. There is currently no effective medical treatment for GM1 gangliosidosis.

The AllStripes GM1 gangliosidosis program is in the pilot stage, in partnership with the Cure GM1 Foundation and the National Tay-Sachs & Allied Diseases Association, to grow knowledge about the condition that could help develop treatments.