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Our AllStripes partners
Patient advocacy organizations
Alliance to Cure Cavernous Malformation
Allo Hope Foundation
BDSRA
CLOVES Syndrome Community
Caring Hands
Children’s Tumor Foundation
Cure GM1 Foundation
Cure IBM
Cure Mito Foundation
Cure Sanfilippo Foundation
Cure VCP Disease, Inc
CurePSP
Cystinosis Research Network
Dreamsickle Kids Foundation
Fabry Support & Information Group
Galactosemia Foundation
GoPI3Ks
IDefine
International Foundation for CDKL5 Research
International Society for Mannosidosis and Related Diseases
Kabuki Syndrome Foundation
Kabuki UK
Love Never Sinks
Lymphangiomatosis & Gorham’s Disease Alliance
MLD Foundation
Metabolic Support UK
Mississippi Metabolics Foundation
MitoAction
Morquio Community
Myositis Support & Understanding
NF2 Biosolutions
National Tay-Sachs & Allied Diseases Association
Organic Acidemia Association
PSP & CBD Foundation
Pompe Alliance
Priest Family, Patient Advocates
SLC6A1 Connect
Sarcoidosis of Long Island
Sickle Cell Reproductive Education Directive (SC RED)
Stand by Eli
Stronger Than Sarcoidosis
The Chandler Project
WonderFIL Smiles
wAIHA Warriors
Life science partners
HemoShear Therapeutics
Novartis Pharmaceuticals Corporation
Penn Medicine
Taysha
The Orphan Disease Center
UCB Pharma
Ultragenyx
Key opinion leaders
Cindy Neunert
Columbia University
Elizabeth Berry-Kravis
Rush University Medical Center
Forbes D. Porter
NICHD
Jemima Albayda
Johns Hopkins Medicine
Jenny Despotovic
Baylor College of Medicine
Kaleb Yohay
NYU Langone
Lynda Polgreen
Lundquist Institute
Marc Patterson
Mayo Clinic
Michele Lambert
Children’s Hospital of Philadelphia
Nicholas Silvestri
University at Buffalo
Pushpa Narayanaswami
Beth Israel Deaconess Medical Center
Rachael Grace
Boston Children’s Hospital
Reza Seyedsadjadi
Consultant - Assistant in Neurology MGH
Thomas Lloyd
Johns Hopkins Medicine
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