Taysha SURF1 Leigh syndrome study

Understanding the natural history of SURF1 Leigh syndrome
Recruitment goal
participants
Launched in
2021
Status
Active
Image
Partner logo

Overview

About our partner: Taysha Gene Therapies was founded in partnership with The University of Texas Southwestern Medical Center (UT Southwestern) to develop and commercialize transformative gene therapy treatments. Taysha strives to develop and commercialize gene therapy treatments.

Taysha has partnered with AllStripes to understand the natural history of SURF1 Leigh syndrome, including: age of onset, severity of disease, range of symptoms and progression, how symptoms are managed, and healthcare utilization.

Study goal

These findings may contribute to Taysha's long term goal of helping treat SURF1 Leigh Syndrome, including working towards a potential gene therapy for SURF1 Leigh syndrome.

Research partners

About AllStripes

AllStripes is a platform that makes it easy for rare disease patients and caregivers to contribute to drug development research from home.

AllStripes improves the speed and design of drug trials by extracting and analyzing research-grade data from de-identified medical records, creating a pool of new knowledge about each rare condition.

Access your records, drive treatment research